Trends and advances in gene therapy delivery and gene editing

CELL AND GENE THERAPY INSIGHTS

May 2020

Trends and advances in gene therapy delivery and gene editing

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Expert Insight

Polymer nanoparticles: potential for efficient, biodegradable, and cost-effective delivery of gene therapy to multiple tissues

Polymer nanoparticles: potential for efficient, biodegradable, and cost-effective delivery of gene therapy to multiple tissues

Timothy Fong, Steven Bodovitz, Kunwoo Lee

High dose systemic gene therapy: emerging trends on safety and efficacy

High dose systemic gene therapy: emerging trends on safety and efficacy

H Stedman, R Herzog, G Gao et al.

Innovator Insight

FectoVIR<sup>®</sup>-AAV: a giant step for AAV large scale manufacturing

FectoVIR^®-AAV: a giant step for AAV large scale manufacturing

A Nyamay'antu, M Hellal, M Porte et al.

Interview

A return to rational capsid design? Predicting the future of AAV vector R&D

A return to rational capsid design? Predicting the future of AAV vector R&D

R Jude Samulski

Next steps in targeting the CNS with AAV-driven gene therapy

Next steps in targeting the CNS with AAV-driven gene therapy

Bruce Goldsmith

Gene editing as a key enabler of allogeneic cell therapy

Gene editing as a key enabler of allogeneic cell therapy

Torsten Meissner

Precise and non-disruptive gene editing based on programmable nickases

Precise and non-disruptive gene editing based on programmable nickases

Manuel Goncalves